A major medical milestone took place in May 2025, when doctors at the Children’s Hospital of Philadelphia used CRISPR-based ...

Reviving an ancient human gene that prevents gout and fatty liver disease, scientists at Georgia State University have marked ...

CRISPR powers everything from gene editing to rapid diagnostics, but how did one of its most versatile branches arise? A new Cell study, “Functional RNA splitting drove the evolutionary emergence of ...

By reactivating a long-lost gene, researchers were able to lower uric acid levels and stop damaging fat accumulation in human ...

The approach is “very exciting,” but one expert says a lot more research is needed, especially around safety, before clinical ...

Researchers report early but encouraging results on an experimental gene-editing treatment for high cholesterol.

CTX310 showed promising safety and efficacy in a small Phase I trial, according to data presented at the American Heart ...

A CRISPR-based gene therapy showed improvement in lipids in difficult-to-treat patients, but one study raised flags after a death last month in a trial of an unrelated gene therapy.